This virtual event is part of the Transforming Pediatric Healthcare series from U.S. News & World Report, developed with ...

A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...

Impella, which J&J touts as the world’s smallest heart pump, has a range of devices used for various heart conditions. Lexeo ...

Qure N.V. (NASDAQ:QURE) surged around 15% in early trading on Friday after the company said it has secured a Type A meeting ...

The use of base editing to generate universal off-the-shelf CAR T cells induced durable remissions -- up to 36 months in one ...

U.K. biotech Ikarovec has teamed up with VectorBuilder to work on an eye disease gene therapy that could be administered in a ...

A new treatment might just be hope for many people living with chronic pain. In a recent preclinical study, researchers ...

A preclinical study uncovered a new gene therapy that targets pain centers in the brain while eliminating the risk of ...

A five-year-old boy who received the world's most expensive drug as a baby has made "incredible progress" and can walk ...

Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...

An update from the phase 2 LEGEND trial shows that the investigational nonviral gene therapy detalimogene voraplasmid has achieved a 62% complete response rate at six months in patients with high-risk ...

A preclinical study uncovered a new gene therapy that targets pain centers in the brain while eliminating the risk of ...